SynDRA canonical compound SYN0004010 — structure-anchored drug synonym record
| Clinical phase | Launched |
|---|---|
| Approval status | Approved · Rx/OTC |
| Primary target(s) | NPC1L1 |
| Mechanism of action | Niemann-Pick C1-like 1 protein antagonist |
| Indication | hypercholesterolemia | hyperlipidemia | hyperlipidemia, hypercholesterolemia, sitosterolemia | sitosterolemia |
| Disease area | endocrinology | endocrinology | endocrinology, metabolism | metabolism |