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MIGALASTAT
SynDRA canonical compound SYN0004048 — structure-anchored drug synonym record
| Clinical phase | Launched |
|---|
| Approval status | Approved · Rx |
|---|
| Primary target(s) | GLA |
|---|
| Mechanism of action | alpha-galactosidase a inhibitor |
|---|
| Indication | fabry disease |
|---|
| Disease area | endocrinology |
|---|
All known targets
- GLA
- AGL
- GAA
- GBA2
- GLB1
- Glb1
- LCT
- Lct
- MGAM
- SI
- aglC
- lacZ
Mechanisms of action (all sources)
- GLA STABILISER
- Alpha-galactosidase A stabiliser
- alpha-galactosidase a inhibitor
- GLA MODULATOR
- GLA PHARMACOLOGICAL CHAPERONE
ATC classes
- A16A · OTHER ALIMENTARY TRACT AND METABOLISM PRODUCTS
Cross-references
Synonyms
- migalastat HCl
- GR181413A
- 1-Deoxygalactonojirimycin hydrochloride
- 1-Deoxygalactonojirimycin
- migalastat hydrochloride
- galafold
- At-1001, gr-181314a
- Galafold
- DDIG
- D-Galactitol, 1,5-dideoxy-1,5-imino
- (2R,3S,4R,5S)-2-(hydroxymethyl)piperidine-3,4,5-triol
- 1,5-Dideoxy-1,5-iminogalactitol
- 2-(Hydroxymethyl)-3,4,5-piperidinetriol hydrochloride
- C4XNY919FW
- 1-deoxygalactonojirimycin
- 1-Deoxygalactostatin
- migalastatum
- RefChem:56444
- 1-deoxygalacto-nojirimycin
- A16AX14
- DTXCID401507205
- NB-DGJ
- 1,5-Dideoxy-1,5-imino-D-galactitol
- Migalastat [INN]
- Migalastat [USAN:INN]
- UNII-C4XNY919FW
- DGJ
- NSC658776
- Tocris-1258
- MIGALASTAT [MI]
- 3,4,5-Piperidinetriol, 2-(hydroxymethyl)-, (2R,3S,4R,5S)-
- Migalastat (USAN/INN)
- MIGALASTAT [USAN]
- MIGALASTAT [WHO-DD]
- D-galacto-1-Deoxynojirimycin
- orb1737999
- SCHEMBL29355275
- GTPL10200
Reported adverse events
- Abdominal pain
- Epistaxis
- Headache
- Nausea
- Back pain
- Cough
- Nasopharyngitis
- Pyrexia
- Urinary tract infection
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