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RISDIPLAM
SynDRA canonical compound SYN0039674 — structure-anchored drug synonym record
| Clinical phase | Phase 2/Phase 3 |
| Approval status | Approved · Rx |
| Primary target(s) | SMN2 |
| Mechanism of action | RNA splicing inhibitor |
All known targets
Mechanisms of action (all sources)
Drug classes
- Neuromuscular Agents
- Peripheral Nervous System Agents
ATC classes
- M09A · OTHER DRUGS FOR DISORDERS OF THE MUSCULO-SKELETAL SYSTEM
Cross-references
Synonyms
- evrysdi
- RG7916
- RO7034067
- RG-7916
- RO-7034067
- Evrysdi
- UNII-76RS4S2ET1
- 76RS4S2ET1
- Risdiplam [INN]
- SCHEMBL17260852
- EX-A2074
- HY-109101
- CS-0039501
- 4H-Pyrido(1,2-a)pyrimidin-4-one, 7-(4,7-diazaspiro(2.5)oct-7-yl)-2-(2,8-dimethylimidazo(1,2-b)pyridazin-6-yl)-
- 2-(2,8-dimethylimidazo[1,2-b]pyridazin-6-yl)-7-(4,7-diazaspiro[2.5]octan-7-yl)-4H-pyrido[1,2-a]pyrimidin-4-one
- RG 7916
- Risdiplamum
- RefChem:57287
- DTXCID601540823
- MFCD31657372
- Risdiplam [USAN]
- Risdiplam?
- Evrysdi (TN)
- Risdiplam (Standard)
- Risdiplam; RG7916
- RISDIPLAM [JAN]
- RISDIPLAM [MI]
- Risdiplam [USAN:INN]
- RISDIPLAM [WHO-DD]
- Risdiplam (JAN/USAN/INN)
- orb1307794
- RISDIPLAM [ORANGE BOOK]
- GTPL11170
- GLXC-20356
- EBC-12887
- WHO 10614
- AKOS040742554
- compound 1 [PMID: 30044619]
Reported adverse events
- Arthralgia
- Rash
- Urinary tract infection
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